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SDS & Science Snapshots (2022-07-10)
In this issue: CRISPR-Cas9 turns 10; The promise of Gene Therapy for Rare Disease and Shwachman-Diamond Syndrome (SDS) Welcome to our...

Eszter Hars, PhD
Jul 10, 2022


SDS & Science Snapshots (2022-07-03)
In this issue: IRDiRC Working Group Recommendations for rare disease patients; The Access to Rare Indications Act could be a game changer...

Eszter Hars, PhD
Jul 3, 2022


A Blast from the Past: Cresta's SDS Story from the US
"I look forward to many more years and to support research to aid SDS patients in the fight against leukemia and Myelodysplastic...

Eszter Hars, PhD
Apr 27, 2022
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