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In this issue: IRDiRC Working Group Recommendations for rare disease patients; The Access to Rare Indications Act could be a game changer...

In this issue: Rare-X report provides update on the true number of rare diseases; new review article on bone marrow failure disorders by...

"I look forward to many more years and to support research to aid SDS patients in the fight against leukemia and Myelodysplastic...