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All Blogs & News
How YOU can help move gene therapy forward for SDS
Gene therapy for SDS is advancing. Learn what's being developed, why base and prime editing matter, and how your perspective can shape what comes next.
Eszter Hars, PhD
Jul 9
One Year Later: The SDS PFDD Voice of the Patient Report Is Published — and Your Voice Is Already at Work
The Shwachman-Diamond Syndrome Voice of the Patient report is now published and submitted to the FDA. Learn what the EL-PFDD meeting captured, how the report is used, and what comes next.
Eszter Hars, PhD
Jun 4
How to Fundraise for Shwachman-Diamond Syndrome Research: A Free Guide for Families and Supporters
SDS Alliance's free fundraising guide helps families and supporters raise funds for Shwachman-Diamond Syndrome research — on their own terms, at any level.
Eszter Hars, PhD
May 30
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